RE: Is it reasonable to add covarite to PD parameters kin or kout?

From: Mike Dodds Date: July 28, 2015 technical Source: mail-archive.com
Li, It's worth pointing out that the typical IDR formulation assumes proportional effect on response. That is, if the drug effect is inhibition of synthesis (e.g Imax=0.5), a subject with baseline 100 will go to 50 and a subject with baseline 1000 will go to 500. If your data is suggesting that a subject with baseline 100 goes to 50 and a subject with baseline 1000 goes to 950, the proportional response formulation is probably a mismatch. Introduction of baseline as a covariate (in this case, with a large negative coefficient?) would align the model with data, but you may instead look at parameterizing the drug effect component of the model differently. Warm Regards, Mike
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From: [email protected] [mailto:[email protected]] On Behalf Of Mats Karlsson Sent: Tuesday, July 28, 2015 3:15 AM To: Peiming Ma; Mark Sale; Zhao,Li; [email protected] Subject: [NMusers] RE: Is it reasonable to add covarite to PD parameters kin or kout? Hi, There are both pros and cons of using baseline observations as a covariate. We presented four different options for how to handle baseline and investigated estimation properties in the paper below. What we didn't look at, because it is a very bad idea, is to use an baseline observation both as a covariate and dependent variable. Approaches to handling pharmacodynamic baseline responses. Dansirikul C, Silber HE, Karlsson MO. J Pharmacokinet Pharmacodyn. 2008 Jun;35(3):269-83. Best regards, Mats Mats Karlsson, PhD Professor of Pharmacometrics Dept of Pharmaceutical Biosciences Faculty of Pharmacy Uppsala University Box 591 75124 Uppsala Phone: +46 18 4714105 Fax + 46 18 4714003 http://www.farmbio.uu.se/research/researchgroups/pharmacometrics/ From: [email protected]<mailto:[email protected]> [mailto:[email protected]] On Behalf Of Peiming Ma Sent: Tuesday, July 28, 2015 3:31 AM To: Mark Sale; Zhao,Li; [email protected]<mailto:[email protected]> Subject: [NMusers] RE: Is it reasonable to add covarite to PD parameters kin or kout? Dear Mark and Li, I think there is nothing wrong with using baseline as a covariate. Baseline observations contain more information than just some pre-treatment observations and thus have a lot of explanatory power; this is the reason they appear significant more often than not. Comparisons after treatments should try to use all information before treatments (thus including baselines). Statisticians habitually use baselines as covariates in their ANCOVA models for obviously good reasons. Regards, Peiming From: [email protected]<mailto:[email protected]> [mailto:[email protected]] On Behalf Of Mark Sale Sent: Tuesday, July 28, 2015 3:34 AM To: Zhao,Li; [email protected]<mailto:[email protected]> Subject: [NMusers] RE: Is it reasonable to add covarite to PD parameters kin or kout? Li, I'm going to go out on a limb (since I haven't seen your data or understand the biology) and suggest that the baseline value is not a covariate, but is just another observation (presumably with drug concentration = 0). The baseline value is sort of by definition a function of kin. So, you might look for predictors of Kin (age? Disease stage?) rather than using the observed value to predict the parameters (which then predict the observed value). Also note that covariates are, by definition, measured without error, and a baseline value is likely measure with error (the same error as any other observation?). Mark From: [email protected]<mailto:[email protected]> [mailto:[email protected]] On Behalf Of Zhao,Li Sent: Monday, July 27, 2015 2:39 PM To: [email protected]<mailto:[email protected]> Subject: [NMusers] Is it reasonable to add covarite to PD parameters kin or kout? Dear NMusers, Right now I am doing covarite analysis for an indirect response model. I tested a few potential covarites and found it's STATISTICALLY significant if I add observed baseline value to kin. But I am not sure if it makes sense to add the baseline value as a covarite to kin. Could you please help me if you have had similar experiences before? Thank you very much!