PK-PD modelling how to FIX the placebo response model

1 messages 1 people Latest: Jul 30, 2010
All, I am working on a PK-PD analysis of longitudinal data in a pain study. I would like to be able make a statement about statistical significance of the treatment effect at the end of the analysis, thus I would like to have some control of the type 1 error by having a pre-specified process for how to do this analysis (although the model may not be 100% pre-specified). The process I am thinking of is: 1. Develop placebo model for longitudinal data based on placebo data. 2. Fix placebo parameters and fit full data set (including also active treatment data). 3. Add concentration effect relationship to model and fit the full data set. 4. Assess whether there was a statistical significant treatment effect by comparing ofv from 2 and 3. 5. Repeat 2 and 3 but without fixing placebo model. My questions are: Is this a sensible approach? If so should I fix only structural parameters related to the placebo model or also random effects parameters of the placebo model? Is step 5 useful? If so what for? Regards, Matts Kågedal, AstraZeneca. -------------------------------------------------------------------------- Confidentiality Notice: This message is private and may contain confidential and proprietary information. If you have received this message in error, please notify us and remove it from your system and note that you must not copy, distribute or take any action in reliance on it. Any unauthorized use or disclosure of the contents of this message is not permitted and may be unlawful.